Drug Type AAV based gene therapy |
Synonyms AAV1-gamma-sarcoglycan gene therapy - Genethon, AAV1-gamma-sarcoglycan vector injection - Genethon, Adeno-associated viral 1 vector-mediated gamma-sarcoglycan gene therapy + [2] |
Target |
Mechanism Gamma-sarcoglycan gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Muscular Dystrophies, Limb-Girdle | Phase 1 | - | - | |
Muscular Dystrophies, Limb-Girdle | Phase 1 | - | - | |
Sarcoglycanopathies | Discovery | FR | - |