Last update 02 Dec 2024

SQY-51

Overview

Basic Info

Drug Type
ASO
Synonyms
SQY 51, SQY51
Target
dystrophin
Mechanism
dystrophin inhibitors(Dystrophin inhibitors), Dystrophin expression stimulants, RNA interference
Therapeutic Areas
Nervous System DiseasesCongenital DisordersSkin and Musculoskeletal Diseases+ [1]
Active Indication
Muscular Dystrophy, Duchenne
Inactive Indication-
Originator Organization
SQYTherapeutics SARLSQYTherapeutics SARL
Active Organization
SQYTherapeutics SARLSQYTherapeutics SARLBiotrial Research SAS
Inactive Organization-
Drug Highest PhasePhase 1/2
First Approval Date-
RegulationOrphan Drug (US)
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Related

1
Clinical Trials associated with SQY-51
NCT05753462 / RecruitingPhase 1/2IIT
Phase 1/2a, Monocentric, Open Label Study to Evaluate the Safety, PK and PD of SQY51 in Paediatric and Adult Patients With a Genetically Confirmed Diagnosis of Duchenne Muscular Dystrophy
100 Clinical Results associated with SQY-51
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100 Translational Medicine associated with SQY-51
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100 Patents (Medical) associated with SQY-51
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100 Deals associated with SQY-51
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Muscular Dystrophy, DuchennePhase 2
FR
Biotrial Research SAS
26 Apr 2023
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

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Clinical Trial

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Approval

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Regulation

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