Drug Type AAV based gene therapy |
Synonyms |
Target |
Mechanism Myotubularin expression stimulants |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Congenital Structural Myopathy | Preclinical | US | 22 Jan 2014 |