Last update 14 Apr 2025

JWK-008

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
JWK 008, JWK008
Target
IDUA
Action
stimulants
Mechanism
IDUA gene stimulants(Alpha-L-iduronidase gene stimulants)
Therapeutic Areas
Congenital DisordersEndocrinology and Metabolic DiseaseSkin and Musculoskeletal Diseases+ [1]
Active Indication
Mucopolysaccharidosis I
Inactive Indication-
Originator Organization
Chengdu Genevector Biotechnology Co. Ltd.Chengdu Genevector Biotechnology Co. Ltd.Startup
Active Organization
West China HospitalWest China HospitalChengdu Genevector Biotechnology Co. Ltd.Chengdu Genevector Biotechnology Co. Ltd.Startup
Inactive Organization-
Drug Highest PhasePhase 1
First Approval Date-
Regulation-
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Related

2
Clinical Trials associated with JWK-008
NCT06519552
/ RecruitingPhase 1IIT
A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 Given by a Single Intravenous Infusion in Patients With Mucopolysaccharidosis Type I
ChiCTR2400079798
/ RecruitingPhase 1IIT
A clinical study evaluating the safety, tolerability, and initial efficacy of JWK008 given by a single intravenous infusion in patients with MPS I
100 Clinical Results associated with JWK-008
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100 Translational Medicine associated with JWK-008
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100 Patents (Medical) associated with JWK-008
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100 Deals associated with JWK-008
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Mucopolysaccharidosis IPhase 1
China
Chengdu Genevector Biotechnology Co. Ltd.Chengdu Genevector Biotechnology Co. Ltd.Startup
15 Jan 2024
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
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Approval

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Regulation

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