Last update 07 Nov 2024

VGM-R02b

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
adeno-associated viral vector 9 delivering human Glutaryl-CoA Dehydrogenase (GCDH) gene, VGM R02b, VGMR02B
Target
GCDH
Mechanism
GCDH stimulants(glutaryl-CoA dehydrogenase stimulants)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersEndocrinology and Metabolic Disease+ [1]
Active Indication
Glutaric Acidemia I
Inactive Indication-
Originator Organization
Shanghai Vitalgen Biopharma Co., Ltd.Shanghai Vitalgen Biopharma Co., Ltd.Startup
Active Organization
Shanghai Vitalgen Biopharma Co., Ltd.Shanghai Vitalgen Biopharma Co., Ltd.Startup
Inactive Organization-
Drug Highest PhasePhase 1
First Approval Date-
RegulationOrphan Drug (US), Orphan Drug (EU)
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Related

2
Clinical Trials associated with VGM-R02b
NCT06217861 / RecruitingPhase 1
An Open-Label, Dose-Escalation and Dose-Expansion Phase I Clinical Study to Evaluate the Tolerability, Safety and Efficacy of VGM-R02b in Patients With Glutaric Acidemia Type I
CTR20234077 / Not yet recruitingPhase 1
一项评估在I型戊二酸血症患者中给予VGM-R02b后的耐受性、安全性和有效性的开放、剂量递增和剂量扩展的I期临床研究
[Translation] An open-label, dose-escalation, and dose-expansion Phase I study evaluating the tolerability, safety, and efficacy of VGM-R02b in patients with glutaric acidemia type I
100 Clinical Results associated with VGM-R02b
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100 Translational Medicine associated with VGM-R02b
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100 Patents (Medical) associated with VGM-R02b
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100 Deals associated with VGM-R02b
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R&D Status

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IndicationHighest PhaseCountry/LocationOrganizationDate
Glutaric Acidemia IPhase 1
CN
Shanghai Vitalgen Biopharma Co., Ltd.Shanghai Vitalgen Biopharma Co., Ltd.Startup
25 Dec 2023
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Clinical Result

Indication
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Approval

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Regulation

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