Drug Type Zinc-finger nucleases |
Synonyms PMP22 gene repression mediated by ZFRs (Sangamo Therapeutics) |
Target |
Mechanism PMP22 inhibitors(peripheral myelin protein 22 inhibitors) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Charcot-Marie-Tooth Disease, Type Ia | Preclinical | US | 07 May 2024 |