Drug Type AAV based gene therapy |
Synonyms XLRS gene therapy-AGTC, rAAV hRS1 (Applied Genetic Technologies Corp.), rAAV2tYF CB hRS1 + [4] |
Target |
Action- |
Mechanism RPGR gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinoschisis | Phase 2 | - | - |