Drug Type Gene therapy, Hematopoietic stem cell therapy |
Synonyms- |
Target- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhaseDiscontinuedPhase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Osteopetrosis, Autosomal Recessive 1 | Phase 1 | US | 19 Nov 2020 | |
Osteopetrosis | Preclinical | SE | - | 07 Mar 2019 |