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Last update 20 Mar 2025
Methylmalonic acidemia(Genespire)
Last update 20 Mar 2025
Overview
Basic Info
Drug Type Gene therapy |
Synonyms- |
Target |
Action- |
Mechanism MUT gene stimulants |
Active Indication |
Inactive Indication- |
Originator Organization  GeneSpire SrlStartup |
Active Organization GeneSpire SrlStartup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Methylmalonic Acidemia | Preclinical | Italy | GeneSpire SrlStartup | 09 May 2024 |
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Clinical Result
Clinical Result
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