Last update 22 Nov 2024

ER-2001

Overview

Basic Info

Drug Type
siRNA
Synonyms
A plasmid encoding a rabies virus glycoprotein tag & lysosome-associated membrane glycoprotein 2 fusion protein gene and a mutant huntingtin small interfering RNA, ER-2001, ER2001
Target
LAMP-2
Mechanism
LAMP-2 modulators(Lysosome-associated membrane glycoprotein 2 modulators)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersOther Diseases
Active Indication
Huntington Disease
Inactive Indication-
Originator Organization
ExoRNA Bioscience Nanjing Co. Ltd.
Active Organization
ExoRNA Bioscience Nanjing Co. Ltd.
Inactive Organization-
Drug Highest PhasePhase 1
First Approval Date-
RegulationOrphan Drug (US)
Login to view timeline

Related

2
Clinical Trials associated with ER-2001
NCT06024265 / RecruitingEarly Phase 1
An Open-Label, Dose Escalation Early Phase 1 Study of ER2001 Intravenous Injection in Adults With Early Manifest Huntington's Disease
CTR20243121 / Not yet recruitingPhase 1
ER2001注射液治疗早期显性亨廷顿舞蹈病的随机、盲法、安慰剂对照的I期临床研究
[Translation] A randomized, blinded, placebo-controlled phase I clinical study of ER2001 injection in the treatment of early-stage dominant Huntington's disease
100 Clinical Results associated with ER-2001
Login to view more data
100 Translational Medicine associated with ER-2001
Login to view more data
100 Patents (Medical) associated with ER-2001
Login to view more data
100 Deals associated with ER-2001
Login to view more data

R&D Status

10 top R&D records.
Login
to view more data
IndicationHighest PhaseCountry/LocationOrganizationDate
Huntington DiseasePhase 1
CN
ExoRNA Bioscience Nanjing Co. Ltd.
20 Aug 2024
Login to view more data

Clinical Result

Indication
Phase
Evaluation
View All Results
Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

No Data

Login to view more data

Translational Medicine

Boost your research with our translational medicine data.
login
or
view full example data
Boost your research with our translational medicine data.

Deal

Boost your decision using our deal data.
login
or
view full example data
Boost your decision using our deal data.

Core Patent

Boost your research with our Core Patent data.
login
or
view full example data
Boost your research with our Core Patent data.

Clinical Trial

Identify the latest clinical trials across global registries.
login
or
view full example data
Identify the latest clinical trials across global registries.

Approval

Accelerate your research with the latest regulatory approval information.
login
or
view full example data
Accelerate your research with the latest regulatory approval information.

Regulation

Understand key drug designations in just a few clicks with Synapse.
login
or
view full example data
Understand key drug designations in just a few clicks with Synapse.
Chat with Hiro
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free