Drug Type AAV based gene therapy |
Synonyms adeno-associated viral vector serotype 2 containing the human SLC6A3 gene |
Target- |
Action- |
Mechanism- |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (European Union) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Parkinsonism-Dystonia, Infantile | Preclinical | United Kingdom | - | |
Parkinsonism-Dystonia, Infantile | Preclinical | United States | - |