Drug Type AAV based gene therapy |
Synonyms SKG 0701, SKG0701 |
Target |
Mechanism ATP7B modulators(ATPase copper transporting beta modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hepatolenticular Degeneration | Preclinical | US | 07 May 2024 |