Drug Type Gene editing |
Synonyms Virus-like particle containing Cas9/gRNA ribonucleoprotein targeting the human HTT gene |
Target |
Mechanism HTT gene modulators |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (EU) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Huntington Disease | Preclinical | CN | 29 Aug 2023 |