Drug Type AAV based gene therapy |
Synonyms- |
Target- |
Action- |
Mechanism- |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Neurodegenerative Diseases | Preclinical | Spain | 28 May 2019 | |
| Anemia, Aplastic | Preclinical | Spain | - | |
| Anemia, Aplastic | Preclinical | Spain | - | |
| Anemia, Aplastic | Preclinical | Switzerland | - | |
| Heart Failure | Preclinical | Spain | - | |
| Heart Failure | Preclinical | Spain | - | |
| Heart Failure | Preclinical | Switzerland | - | |
| Pulmonary Fibrosis | Preclinical | Spain | - | |
| Pulmonary Fibrosis | Preclinical | Spain | - | |
| Pulmonary Fibrosis | Preclinical | Switzerland | - |





