Drug Type AAV based gene therapy |
Synonyms HUB-101, HUB101 |
Target |
Mechanism KCNJ13 gene modulators |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization- |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Preclinical | US | 30 Jan 2022 |