Drug Type Enzyme |
Synonyms GAAM6P, M 021, M021 |
Target |
Action- |
Mechanism Alpha glucosidase replacements, Enzyme replacements |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationRare Pediatric Disease (United States) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Glycogen Storage Disease Type II | Preclinical | United States | 01 Feb 2022 |