Drug Type AAV based gene therapy |
Synonyms- |
Target |
Action inhibitors |
Mechanism AIPL1 inhibitors(aryl hydrocarbon receptor interacting protein like 1 inhibitors), Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Leber Congenital Amaurosis | Discovery | Italy | - |