Drug Type Oligonucleotide |
Synonyms- |
Target |
Action modulators |
Mechanism CLN3 modulators(Battenin modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
License Organization- |
Drug Highest PhaseDiscovery |
First Approval Date- |
Regulation- |

| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Arrhythmias, Cardiac | Discovery | - | 14 Jul 2022 | |
| Other Diseases | Discovery | - | 14 Jul 2022 | |
| Retinal Degeneration | Discovery | - | 14 Jul 2022 |





