Last update 01 Nov 2024

CLN2 gene therapy(REGENXBIO, Inc.)

Overview

Basic Info

Drug Type
Gene therapy
Synonyms-
Target
TPP1
Mechanism
TPP1 gene transference(Tripeptidyl Peptidase 1 gene transference)
Therapeutic Areas
Nervous System DiseasesCongenital DisordersEndocrinology and Metabolic Disease+ [1]
Active Indication
Neuronal Ceroid-Lipofuscinoses
Inactive Indication-
Originator Organization
RegenxBio, Inc.RegenxBio, Inc.
Active Organization
Weill Medical College of Cornell UniversityWeill Medical College of Cornell UniversityRegenxBio, Inc.RegenxBio, Inc.
Inactive Organization-
Drug Highest PhasePhase 2
First Approval Date-
Regulation-
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Related

100 Clinical Results associated with CLN2 gene therapy(REGENXBIO, Inc.)
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100 Translational Medicine associated with CLN2 gene therapy(REGENXBIO, Inc.)
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100 Patents (Medical) associated with CLN2 gene therapy(REGENXBIO, Inc.)
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100 Deals associated with CLN2 gene therapy(REGENXBIO, Inc.)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Neuronal Ceroid-LipofuscinosesPhase 2-
Weill Medical College of Cornell UniversityWeill Medical College of Cornell University
-
Neuronal Ceroid-LipofuscinosesPhase 2-
RegenxBio, Inc.RegenxBio, Inc.
-
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Clinical Result

Indication
Phase
Evaluation
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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