Drug Type mRNA |
Synonyms modified human ATP binding cassette subfamily B member 4 (ABCB4) mRNA encoding multidrug resistance protein 3 (MDR3) |
Target |
Mechanism MDR3 modulators(Multidrug resistance protein 3 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationRare Pediatric Disease (US), Orphan Drug (US) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
progressive familial intrahepatic cholestasis | Preclinical | CN | 01 Nov 2024 |