Drug Type AAV based gene therapy |
Synonyms AAV-based bestrophin 1 gene therapy (NightstaRx), NSR-BEST1 |
Target |
Mechanism BEST1 modulators(Bestrophin-1 modulators) |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Vitelliform Macular Dystrophy | Discovery | GB | 05 Nov 2015 |