Drug Type AAV based gene therapy |
Synonyms LTGT06 |
Target |
Mechanism ATP7A modulators(ATPase copper transporting alpha modulators), Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Inactive Organization- |
Drug Highest PhaseEarly Phase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Menkes Kinky Hair Syndrome | Phase 1 | CN | 18 Apr 2022 |