Drug Type CRISPR/Cas |
Synonyms factor VIII CRISPR/Cas9-gene therapy (Casebia) |
Target |
Mechanism Factor VIII gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization Casebia Therapeutics LLCStartup |
Active Organization Casebia Therapeutics LLCStartup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Hemophilia A | Preclinical | US | Casebia Therapeutics LLCStartup | - |