Drug Type Small molecule drug |
Synonyms- |
Target |
Mechanism ABCD1 modulators(ATP Binding Cassette Subfamily D Member 1 modulators), ABCD2 modulators(ATP binding cassette subfamily D member 2 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization ![]() |
Active Organization ![]() |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Adrenoleukodystrophy | Preclinical | US | ![]() | 01 Dec 2024 |