Drug Type Gene therapy |
Synonyms- |
Target |
Mechanism Glucosylceramidase replacements, Gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhaseDiscontinuedPhase 1 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Gaucher Disease | Phase 1 | - | - |