Drug Type AAV based gene therapy |
Synonyms- |
Target |
Mechanism ACADVL modulators(acyl-CoA dehydrogenase very long chain modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization Kriya Therapeutics, Inc.Startup |
Active Organization Kriya Therapeutics, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
VLCAD Deficiency | Preclinical | US | Kriya Therapeutics, Inc.Startup | - |