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Last update 20 Mar 2025
Hereditary inclusion body myopathy gene therapy(Gradalis, Inc.)
Last update 20 Mar 2025
Overview
Basic Info
Drug Type Gene therapy |
Synonyms GNE Lipoplex, Hereditary inclusion body myopathy gene therapy |
Target |
Action- |
Mechanism GNE gene transference |
Therapeutic Areas |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingPhase 1 |
First Approval Date- |
RegulationOrphan Drug (United States) |
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R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Distal Myopathies | Phase 1 | - | - | |
| Distal Myopathy, Nonaka Type | Phase 1 | United States | - |
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Clinical Result
Clinical Result
Indication
Phase
Evaluation
View All Results
Not Applicable | - | lmvufrjlwh(rzvcampofu) = nrutvtyalx kvycafzybx (anvhjsptbd ) | - | 01 May 2010 |
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