Drug Type AAV based gene therapy |
Synonyms |
Target |
Action- |
Mechanism RPE65 gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinitis Pigmentosa | Phase 2 | France | 20 Nov 2018 | |
Leber Congenital Amaurosis | Phase 2 | - | - |