Last update 23 Jan 2025

PLX-200

Overview

Basic Info

Drug Type
Small molecule drug
Synonyms
Target
TPP1
Mechanism
TPP1 stimulants(Tripeptidyl Peptidase 1 stimulants), Apoptosis inhibitors
Therapeutic Areas
Nervous System DiseasesCongenital DisordersEndocrinology and Metabolic Disease+ [1]
Active Indication
Neuronal Ceroid-LipofuscinosesTay-Sachs DiseaseSandhoff Disease
Inactive Indication
Leukodystrophy, Globoid Cell
Originator Organization
Rush University Medical CenterRush University Medical Center
Active Organization
Polaryx Therapeutics, Inc.Polaryx Therapeutics, Inc.Startup
Inactive Organization-
Drug Highest PhasePhase 3
First Approval Date-
RegulationOrphan Drug (EU), Fast Track (US)
Login to view timeline

Related

1
Clinical Trials associated with PLX-200
NCT04637282
/ Not yet recruitingPhase 3
A Randomized. Multicenter, Double-Blind, Placebo-Controlled Safety, Tolerability, and Efficacy Study of PLX-200 in Participants With Mild-to-Moderate Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) Disease
100 Clinical Results associated with PLX-200
Login to view more data
100 Translational Medicine associated with PLX-200
Login to view more data
100 Patents (Medical) associated with PLX-200
Login to view more data
100 Deals associated with PLX-200
Login to view more data

R&D Status

10 top R&D records.
Login
to view more data
IndicationHighest PhaseCountry/LocationOrganizationDate
Neuronal Ceroid-LipofuscinosesPhase 3-
Polaryx Therapeutics, Inc.Polaryx Therapeutics, Inc.Startup
01 Dec 2024
Tay-Sachs DiseasePreclinical
US
Polaryx Therapeutics, Inc.Polaryx Therapeutics, Inc.Startup
28 Sep 2021
Sandhoff DiseasePreclinical
US
Polaryx Therapeutics, Inc.Polaryx Therapeutics, Inc.Startup
27 Aug 2021
Leukodystrophy, Globoid CellDiscovery
US
Polaryx Therapeutics, Inc.Polaryx Therapeutics, Inc.Startup
17 Aug 2021
Login to view more data

Clinical Result

Indication
Phase
Evaluation
View All Results
Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date

No Data

Login to view more data

Translational Medicine

Boost your research with our translational medicine data.
login
or
view full example data
Boost your research with our translational medicine data.

Deal

Boost your decision using our deal data.
login
or
view full example data
Boost your decision using our deal data.

Core Patent

Boost your research with our Core Patent data.
login
or
view full example data
Boost your research with our Core Patent data.

Clinical Trial

Identify the latest clinical trials across global registries.
login
or
view full example data
Identify the latest clinical trials across global registries.

Approval

Accelerate your research with the latest regulatory approval information.
login
or
view full example data
Accelerate your research with the latest regulatory approval information.

Regulation

Understand key drug designations in just a few clicks with Synapse.
login
or
view full example data
Understand key drug designations in just a few clicks with Synapse.
Chat with Hiro
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free