Drug Type AAV based gene therapy |
Synonyms triple capsid mutant based NAGLU gene therapy (Lacerta Therapeutics/University of Florida) |
Target- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Mucopolysaccharidosis III | Preclinical | US | Lacerta Therapeutics, Inc.Startup | - |
Mucopolysaccharidosis III | Preclinical | US | - |