Drug Type AAV based gene therapy |
Synonyms adeno-associated virus vector based gene therapy (Adverum/ Editas Medicine) |
Target- |
Action- |
Mechanism Gene transference |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization |
Active Organization |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
RegulationOrphan Drug (United States) |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Retinal Dystrophies | Preclinical | United States | - | |
Retinal Diseases | Discovery | United States | - | |
Retinal Diseases | Discovery | United States | - |