Drug Type AAV based gene therapy |
Synonyms- |
Target- |
Mechanism Gene transference |
Active Indication- |
Inactive Indication |
Originator Organization |
Active Organization- |
Inactive Organization |
Drug Highest PhasePendingDiscovery |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Wolman Disease | Discovery | US | - |