Drug Type AAV based gene therapy |
Synonyms PMD (Myrtelle) |
Target |
Mechanism PLP1 modulators(proteolipid protein 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization ![]() |
Active Organization ![]() |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Pelizaeus-Merzbacher Disease | Preclinical | US | ![]() | 25 Apr 2024 |