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Last update 20 Mar 2025
Pelizaeus-Merzbacher Disease (Myrtelle)
Last update 20 Mar 2025
Overview
Basic Info
Drug Type AAV based gene therapy |
Synonyms PMD (Myrtelle) |
Target |
Action modulators |
Mechanism PLP1 modulators(proteolipid protein 1 modulators) |
Therapeutic Areas |
Active Indication |
Inactive Indication- |
Originator Organization  Myrtelle, Inc.Startup |
Active Organization Myrtelle, Inc.Startup |
Inactive Organization- |
Drug Highest PhasePreclinical |
First Approval Date- |
Regulation- |
R&D Status
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| Indication | Highest Phase | Country/Location | Organization | Date |
|---|---|---|---|---|
| Pelizaeus-Merzbacher Disease | Preclinical | United States | Myrtelle, Inc.Startup | 25 Apr 2024 |
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Clinical Result
Clinical Result
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