Knowledge Base

What is somatic gene therapy?

8 December 2023
2 min read

Somatic cell gene therapy targets those cells of the body that are not involved in reproduction – the somatic cells. Examples include the cells that make up the retina, liver, or heart. Somatic cell gene therapies are being developed for a wide-range of diseases, but most gene therapies are not yet FDA approved for widespread use. Patients currently receiving somatic gene therapy do so through clinical trials which are subject to FDA oversight.

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