Last update 21 Nov 2024

OTOF-GT gene therapy(Sensorion SAS)

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
A dual vector gene therapy product containing AAV8 vectors expressing the 5¿ and 3¿ portion of human otoferlin (OTOF) gene, Adeno‐associated viral vector serotype 8 containing the 3' human otoferlin coding sequence, adeno‐associated viral vector serotype 8 containing the 5' human otoferlin coding sequence, OTOF-GT
+ [1]
Target
Mechanism
OTOF modulators(otoferlin modulators), Gene transference
Inactive Indication-
Originator Organization
Active Organization
Inactive Organization-
Drug Highest PhasePhase 1/2
First Approval Date-
RegulationRare Pediatric Disease (US), Orphan Drug (EU)
Login to view timeline

R&D Status

10 top R&D records.
Login
to view more data
IndicationHighest PhaseCountry/LocationOrganizationDate
DeafnessPhase 2
FR
21 Jun 2024
DeafnessPhase 2
AU
21 Jun 2024
Hearing Loss, SensorineuralPhase 2
FR
21 Jun 2024
Hearing Loss, SensorineuralPhase 2
AU
21 Jun 2024
Hearing DisordersPhase 1--
Hearing LossIND Application
DE
19 Jul 2023
Hearing LossIND Application
IT
19 Jul 2023
Login to view more data

Clinical Result

Indication
Phase
Evaluation
View All Results
Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 1/2
1
(dvfduzxrrj) = The surgery was well tolerated by the patient and no safety signals were reported. mgejrlssmk (uuafdicrzb )
Positive
20 Sep 2024
Login to view more data

Translational Medicine

Boost your research with our translational medicine data.
Boost your research with our translational medicine data.

Deal

Boost your decision using our deal data.
Boost your decision using our deal data.

Core Patent

Boost your research with our Core Patent data.
Boost your research with our Core Patent data.

Clinical Trial

Identify the latest clinical trials across global registries.
Identify the latest clinical trials across global registries.

Approval

Accelerate your research with the latest regulatory approval information.
Accelerate your research with the latest regulatory approval information.

Regulation

Understand key drug designations in just a few clicks with Synapse.
Understand key drug designations in just a few clicks with Synapse.
Chat with Hiro
Get started for free today!
Accelerate Strategic R&D decision making with Synapse, PatSnap’s AI-powered Connected Innovation Intelligence Platform Built for Life Sciences Professionals.
Start your data trial now!
Synapse data is also accessible to external entities via APIs or data packages. Empower better decisions with the latest in pharmaceutical intelligence.
Bio
Bio Sequences Search & Analysis
Sign up for free
Chemical
Chemical Structures Search & Analysis
Sign up for free