Last update 12 Apr 2025

HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)

Overview

Basic Info

Drug Type
Gene therapy
Synonyms-
Target
HBG1 x HBG2
Action
stimulants, agonists
Mechanism
HBG gene stimulators, HBG2 agonists(hemoglobin subunit gamma 2 agonists)
Therapeutic Areas
Congenital DisordersHemic and Lymphatic DiseasesOther Diseases
Active Indication-
Inactive Indication
Anemia, Sickle CellBeta-Thalassemia
Originator Organization
St. Jude Children's Research Hospital, Inc.St. Jude Children's Research Hospital, Inc.The Children's Hospital Corp.The Children's Hospital Corp.
Active Organization-
Inactive Organization
St. Jude Children's Research Hospital, Inc.St. Jude Children's Research Hospital, Inc.The Children's Hospital Corp.The Children's Hospital Corp.
Drug Highest PhasePendingPreclinical
First Approval Date-
Regulation-

Related

100 Clinical Results associated with HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)
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100 Translational Medicine associated with HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)
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100 Patents (Medical) associated with HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)
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1
Literatures (Medical) associated with HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)
12 Nov 2019Blood advancesQ2 · MEDICINE
Genome editing of HBG1 and HBG2 to induce fetal hemoglobin
Q2 · MEDICINE
100 Deals associated with HBG1/HBG2 gene therapy (St. Jude Children 's Research Hospital)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Anemia, Sickle CellPreclinical
United States
St. Jude Children's Research Hospital, Inc.St. Jude Children's Research Hospital, Inc.
06 Nov 2019
Anemia, Sickle CellPreclinical
United States
The Children's Hospital Corp.The Children's Hospital Corp.
06 Nov 2019
Beta-ThalassemiaPreclinical
United States
St. Jude Children's Research Hospital, Inc.St. Jude Children's Research Hospital, Inc.
06 Nov 2019
Beta-ThalassemiaPreclinical
United States
The Children's Hospital Corp.The Children's Hospital Corp.
06 Nov 2019
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Clinical Result

Indication
Phase
Evaluation
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Phase
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Approval

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Regulation

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