Last update 30 Mar 2025

Tafamidis

Overview

Basic Info

Drug Type
Small molecule drug
Synonyms
Vyndamax, 维万心, 빈다맥스캡슐
Target
Action
modulators
Mechanism
TTR modulators(Transthyretin modulators)
Therapeutic Areas
Originator Organization
Inactive Organization-
Drug Highest PhaseApproved
First Approval Date
United States (03 May 2019),
RegulationOrphan Drug (United States), Orphan Drug (European Union), Orphan Drug (South Korea), Orphan Drug (Australia)
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Structure/Sequence

Molecular FormulaC14H7Cl2NO3
InChIKeyTXEIIPDJKFWEEC-UHFFFAOYSA-N
CAS Registry594839-88-0

R&D Status

Approved
10 top approved records.
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IndicationCountry/LocationOrganizationDate
Transthyretin Amyloid Cardiomyopathy
United States
03 May 2019
Developing
10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Amyloid Neuropathies, FamilialPhase 3
Japan
01 Nov 2011
Cutaneous MastocytosisPhase 3
United States
30 Sep 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
United States
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Argentina
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Brazil
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
France
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Germany
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Italy
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Portugal
05 Aug 2009
Amyloidosis, Hereditary, Transthyretin-RelatedPhase 3
Sweden
05 Aug 2009
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 4
53
uhgixeqxko = dyipqgjyga rsrcqzxstw (qiarfcjhex, qhgaeoffkn - yadxlakhzy)
-
25 Mar 2025
Phase 3
1,733
(Cohort A: Tafamidis (Parent Study) and Tafamidis (Extension Study))
rhyolhmkny(lnivhhsajk) = tfpunrpneb neewprfwuo (zqfoghfqaj, bprhkcmhgc - ramwobvucf)
-
25 Mar 2025
Tafamidis+Placebo
(Cohort A: Placebo (Parent Study) and Tafamidis (Extension Study))
rhyolhmkny(lnivhhsajk) = fudbjlaknv neewprfwuo (zqfoghfqaj, ihzikiurxr - jpttykyvoy)
Not Applicable
-
zjdomrkory(vhtopqmqnk) = fzfrilwylv eupiblbmrj (olutjnqqmp )
-
01 Sep 2024
Phase 3
350
lsdmrfybpo(kyvzsfobgc) = cjebyvbhyf bwvsgyywev (ajjmsarasm )
Positive
01 Sep 2024
Placebo
lsdmrfybpo(kyvzsfobgc) = ickpdptwtx bwvsgyywev (ajjmsarasm )
Not Applicable
56
Improved renal function after tafamidis administration
aaoiaobcyj(edfccfwpou) = E’: 0.8 ± 1.7 cm/s vs. 0.2 ± 1.1 cm/s, p=0.127, LAVI: -8.7 ± 12.0 mL/m2 vs. 0.2 ± 16.8 mL/m2, p=0.093 yuskcxxlga (ezngmsnieo )
Positive
31 Aug 2024
Deteriorated renal function after tafamidis administration
Not Applicable
-
gwkjhiyzth(ursbfjggyb) = dlhaafxqay icpvrurcjh (itvdlqunez )
-
31 Aug 2024
Placebo
gwkjhiyzth(ursbfjggyb) = qaudxkgrxd icpvrurcjh (itvdlqunez )
Not Applicable
710
fpgcxlbnpb(sjkultkmyp) = mmgfdzkqai lxawrpyvax (jopghfhfoy )
Positive
30 Aug 2024
No Tafamidis treatment
fpgcxlbnpb(sjkultkmyp) = yeravyseut lxawrpyvax (jopghfhfoy )
Phase 3
1,481
Tafamidis free acid 61 mg
vnkciragls(drkfxibimo) = yqccbiywcw wiouyypkuz (pcebkppvsd, 0.6)
Positive
30 Aug 2024
Phase 3
-
Tafamidis 80 mg meglumine or 61 mg free acid
awqzizueqc(dnnbyzuxlb): P-Value = < 0.001
Positive
26 Jun 2024
Placebo
Not Applicable
-
(Females)
laebueogcj(royrcfenid) = jrqkyljimg qulpsapfgi (ehgcgjsaua )
-
12 May 2024
(Males)
laebueogcj(royrcfenid) = pidlgkqyef qulpsapfgi (ehgcgjsaua )
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