Drug Type ASO |
Synonyms Lademirsen sodium + [3] |
Target |
Mechanism miR-21 inhibitors(microRNA 21 inhibitors) |
Therapeutic Areas |
Active Indication |
Inactive Indication |
Originator Organization |
Active Organization |
Inactive Organization |
Drug Highest PhasePhase 2 |
First Approval Date- |
Regulation- |
Indication | Highest Phase | Country/Location | Organization | Date |
---|---|---|---|---|
Nephritis | Phase 2 | - | - | |
Nephritis | Phase 2 | - | - | |
Nephritis, Hereditary | Preclinical | US | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | DE | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | GB | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | AU | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | FR | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | CN | 02 Nov 2019 | |
Nephritis, Hereditary | Preclinical | ES | 02 Nov 2019 |
Phase 2 | Nephritis, Hereditary microRNA-21 | 43 | uybqrwjhmo(fjfcqhbzvm) = All participants in both groups developed treatment-emergent adverse events (TEAEs), mainly respiratory tract infections, headache, dizziness, metabolic/electrolyte disturbances, and anemia. Treatment was discontinued in three lademirsen-treated participants in the double-blind period, and one participant in the open-label period, owing to TEAEs. lyzmfunxpa (gtljbwteam ) | Negative | 03 Jun 2024 | ||
Placebo |