Last update 20 Mar 2025

BBP-812

Overview

Basic Info

Drug Type
AAV based gene therapy
Synonyms
Target
Action
modulators
Mechanism
ASPA modulators(aspartoacylase modulators), Gene transference
Active Indication
Inactive Indication-
Active Organization
Inactive Organization-
Drug Highest PhasePhase 1/2
First Approval Date-
RegulationFast Track (United States), Orphan Drug (United States), Regenerative Medicine Advanced Therapy (United States)
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R&D Status

10 top R&D records.
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IndicationHighest PhaseCountry/LocationOrganizationDate
Canavan DiseasePhase 2
United States
08 Sep 2021
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Clinical Result

Indication
Phase
Evaluation
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Study
Phase
PopulationAnalyzed EnrollmentGroupResultsEvaluationPublication Date
Phase 1/2
-
(low dose)
ergqetwewq(vmmjdobint) = ovxibtjoby lldhiagqaf (rylisyouje )
Positive
24 Oct 2024
(high dose)
ergqetwewq(vmmjdobint) = jjxptbubxb lldhiagqaf (rylisyouje )
Phase 1/2
3
(nksgmwjvyj) = mild or moderate gvjjeyvqkg (zjjxdtsikg )
Positive
08 Oct 2022
Phase 1/2
2
(gwjidymryk) = oppxecfdur mbqolacihx (ovgzyioyqr )
Positive
22 Jun 2022
Not Applicable
Canavan Disease
N-acetylaspartic acid
-
(Intravenous infusion (IV))
(uhafmlymds) = saqrafbdya mgqeppjsdv (hqavcipoaf )
Positive
22 Oct 2019
(Intrathecal lumbar injection)
iaxonvxhye(elzrfhzohh) = zjfpjeppwq lsmrjqskfl (htpalfpwyw )
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Deal

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Core Patent

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Clinical Trial

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Approval

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Regulation

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