News
AcquisitionExecutive Change
Ultragenyx Announces First Patient Dosed in Aurora Study Evaluating GTX-102 in Additional Angelman Syndrome Genotypes and Age Groups
Orphan DrugFast TrackBreakthrough TherapyOligonucleotide
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ImmunotherapyVaccineCell Therapy
Novartis completes acquisition of Tourmaline Bio
Acquisition
Acquisition
SpringWorks Therapeutics Announces Publication of Long-Term Efficacy and Safety Data from the Phase 3 DeFi Trial of OGSIVEO® (nirogacestat) in Adults with Desmoid Tumors in the Journal of Clinical Oncology
Clinical ResultASCOOrphan DrugDrug Approval
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Patent Expiration