Synonyms Globin abnormality, Globin abnormality, NOS, HEMOGLOBIN DISORDER + [50] |
Introduction A group of inherited disorders characterized by structural alterations within the hemoglobin molecule. |
Target |
Mechanism ACVR2A modulators [+1] |
Active Org. |
Originator Org. |
Active Indication |
Inactive Indication |
Drug Highest PhaseApproved |
First Approval Ctry. / Loc. US |
First Approval Date26 Mar 2024 |
Target |
Mechanism C5 inhibitors |
Active Org. |
Originator Org. |
Active Indication |
Inactive Indication |
Drug Highest PhaseApproved |
First Approval Ctry. / Loc. CN |
First Approval Date06 Feb 2024 |
Target- |
Mechanism BCL11A inhibitors [+1] |
Active Org. |
Originator Org. |
Active Indication |
Inactive Indication- |
Drug Highest PhaseApproved |
First Approval Ctry. / Loc. GB |
First Approval Date16 Nov 2023 |
Start Date01 May 2025 |
Sponsor / Collaborator |
Start Date03 Apr 2025 |
Sponsor / Collaborator |
Start Date01 Apr 2025 |
Sponsor / Collaborator |